Sanofi has added another string to its Pompe disease therapy bow, after getting FDA approval for Nexviazyme, its latest therapy for the rare, inherited disorder. The US regulator has approved ...
Astellas has licensed rights to a drug developed by Selecta Biosciences that could make more patients eligible for treatment with its gene therapy for inherited neuromuscular disorder Pompe disease.
Sherri Gordon, CLC is a certified professional life coach, author, and journalist covering health and wellness, social issues, parenting, and mental health. She also has a certificate of completion ...
The Willem Pompe Institute of Criminal Law and Criminology is the Institute of Criminal Law of Utrecht University’s Faculty of Law, Economics and Governance. Members of staff of this department ...
Pompe disease (PD) is a potentially lethal illness involving irreversible muscle damage resulting from glycogen storage in muscle fiber and activation of autophagic pathways. A promising therapeutic ...
Cherche 1 ou 2 neurologues libéraux pour succession d’une grosse clientèle en vue d’un départ à la retraite fin 2025, dans une grande clinique très agréable à Montpellier disposant d’un plateau ...
Not just my usual body ache and pain caused by the symptoms of living with Pompe disease, but every breath I take feels like it is a real effort and struggle.
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